mostly in Africa or the Eastern Mediterranean

Both sickle cell disease and thalassemia are caused by mistakes in the genes that carry hemoglobin.Middle Eastern and Indian descent.

Britains regulator said its decision to authorize the gene therapy for sickle cell disease was based on a study done on 29 patients.The use of the word cure in relation to sickle cell disease or thalassemia has.Gene therapy treatments can cost millions of dollars and experts have previously raised concerns that they could remain out of reach for the people who would benefit most.

Vertex Pharmaceuticals said it had not yet established a price for the treatment in Britain and was working with health authorities to secure reimbursement and access for eligible patients as quickly as possible.Patients must be hospitalized at least twice once for the collection of the stem cells and then to receive the altered cells.

in a move that could offer relief to thousands of people with the crippling disease in the U.

which won its makers a Nobel Prize in 2020.Inside North Korea 47 photos Were highly confident this was a test of an advanced nuclear device.

Defense Secretary James Mattis warned the North on Sunday that.President Trump threatened to halt all trade with countries doing business with the North.

President Moon Jae-ins national security director.asked by a reporter in Washington if he would attack the North.